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Leber Congenital Amaurosis

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Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023

Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023

Leber Congenital Amaurosis Trial (HG004)

Not yet recruiting
  • Leber Congenital Amaurosis
  • (no location specified)
Jun 13, 2023

Leber Congenital Amaurosis Associated With Mutations in RPE65

Recruiting
  • Leber Congenital Amaurosis
    • Ann Arbor, Michigan
    • +1 more
    Apr 7, 2022

    To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)

    Not yet recruiting
    • To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
    • (no location specified)
    Aug 29, 2023

    Leber Congenital Amaurosis 10, Inherited Retinal Dystrophies, Eye Diseases, Hereditary Trial in United States (EDIT-101)

    Active, not recruiting
    • Leber Congenital Amaurosis 10
    • +6 more
    • Miami, Florida
    • +4 more
    Dec 2, 2022

    Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia

    Active, not recruiting
    • Inherited Retinal Dystrophy Due to RPE65 Mutations
    • Leber Congenital Amaurosis
    • AAV2-hRPE65v2,voretigene neparvovec-rzyl
    • Iowa City, Iowa
    • +1 more
    Dec 9, 2021

    Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia, Ghent (QR-110)

    Active, not recruiting
    • Leber Congenital Amaurosis 10
    • +9 more
    • Iowa City, Iowa
    • +2 more
    Feb 8, 2022

    Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen, Sham)

    Active, not recruiting
    • Leber Congenital Amaurosis 10
    • +9 more
    • Iowa City, Iowa
    • +13 more
    Mar 2, 2022

    Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen)

    Recruiting
    • Leber Congenital Amaurosis 10
    • +10 more
    • Ghent, Belgium
    • +8 more
    Mar 24, 2022

    Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)

    Active, not recruiting
    • Amaurosis of Leber
    • Retinal Diseases
    • rAAV2-CBSB-hRPE65
    • Gainesville, Florida
    • +1 more
    Dec 13, 2021

    Natural History Study of CEP290-Related Retinal Degeneration

    Completed
    • Blindness
    • +7 more
      • Miami, Florida
      • +6 more
      May 18, 2022

      Leber Congenital Amaurosis Trial in Ann Arbor, London (AAV RPE65)

      Completed
      • Leber Congenital Amaurosis
      • AAV RPE65
      • Ann Arbor, Michigan
      • +1 more
      Jun 17, 2021

      Leber Congenital Amaurosis Trial in Philadelphia (voretigene neparvovec-rzyl)

      Completed
      • Leber Congenital Amaurosis
      • voretigene neparvovec-rzyl
      • Philadelphia, Pennsylvania
        The Children's Hospital of Philadelphia
      Oct 30, 2020

      Leber's Congenital Amaurosis Trial in Iowa City, Philadelphia, Ghent (QR-110)

      Completed
      • Leber's Congenital Amaurosis
      • Iowa City, Iowa
      • +2 more
      Oct 13, 2020

      Rare Disorders, Undiagnosed Disorders, Disorders of Unknown Prevalence Trial in Sioux Falls, Sydney

      Recruiting
      • Rare Disorders
      • +309 more
        • Sioux Falls, South Dakota
        • +1 more
        Jun 20, 2022

        Choroideremia Trial in Edmonton (rAAV2.REP1 vector)

        Completed
        • Choroideremia
        • rAAV2.REP1 vector
        • Edmonton, Alberta, Canada
          University of Alberta
        May 16, 2022

        Clinical Presentation of Genetic Disorders in Patients Attending

        Not yet recruiting
        • Genetic Disease Clinical Presentation in Patients Attending Genetics Outpatient Clinic of Assiut University Children Hospital
          • (no location specified)
          Jun 2, 2023

          Leber Congenital Amaurosis, Retinitis Pigmentosa Trial in Beijing (Human primary Retinal Pigment Epithelial (HuRPE) cells)

          Unknown status
          • Leber Congenital Amaurosis, Retinitis Pigmentosa
          • Human primary Retinal Pigment Epithelial (HuRPE) cells
          • Beijing, China
            Beijing Tongren Hospital
          Aug 7, 2018

          Cell Collection to Study Eye Diseases

          Recruiting
          • Retinal Disease
          • +3 more
            • Bethesda, Maryland
              National Institutes of Health Clinical Center
            Jan 23, 2023

            Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in United States (AAV2-hRPE65v2,voretigene

            Active, not recruiting
            • Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
            • AAV2-hRPE65v2,voretigene neparvovec-rzyl
            • Los Angeles, California
            • +9 more
            Oct 22, 2021

            Leber Hereditary Optic Neuropathy Trial in Wuhan (rAAV2-ND4)

            Active, not recruiting
            • Leber Hereditary Optic Neuropathy
            • Wuhan, Hubei, China
              Department of Ophthalmology,Tongji Hospital, Tongji Medical Coll
            Sep 15, 2020

            Retinitis Pigmentosa Trial in Bangkoknoi (BM-MSC)

            Completed
            • Retinitis Pigmentosa
            • BM-MSC
            • Bangkoknoi, Bangkok, Thailand
              Siriraj Hospital Mahidol University
            Aug 31, 2021

            Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

            Active, not recruiting
            • Inherited Retinal Dystrophy Due to RPE65 Mutations
            • AAV2-hRPE65v2
            • (no location specified)
            Dec 9, 2021

            Leber Congenital Amaurosis Trial in Jerusalem (rAAV2-hRPE65)

            Completed
            • Leber Congenital Amaurosis
            • rAAV2-hRPE65
            • Jerusalem, Israel
              Hadassah Medical Organization
            Apr 8, 2018